Zolgensma the worlds most expensive drug at £1.8 million was approved by the NHS on March 8th 2021 after successful trials in U.S. & across Europe. The full qualifying criteria is due to be published by NICE (National Institute for Health & Care).
The benefits of Zolgensma for Haris are described as remarkable and there is strong evidence to support significant milestones being achieved by SMA Type 1 patients.